A patient-centric approach

Hand-in-hand with patients and their families, CAYR rescues and repositions therapeutics for ultra-orphan diseases, thus accelerating treatments for underserved patients. Every effort is made to drive the patients' interest first: ensuring safety, maximizing medical benefits, and ensuring access to care. For CAYR, patient organizations are critical in creating the awareness needs to understand the diseases we develop in. We work with established patient networks and research institutions to identify and validate therapeutics across every stage of development